Login
Create An Account
Login
Create An Account
Search
View All
View All
All Categories
Critical Care, Anaesthetics & Emergency Medicine
Gerontology, Lifestyle Disease & Healthy Aging
Infectious Diseases, Vaccines & Antimicrobials
Ophthalmology
Paediatrics & Neonatology
What's the Diagnosis
Healthcare Alerts
Disease Outbreak Resources »
Cholera Outbreak Resources & Updates
Healthcare Market Analysis & Reports
Special Coverage & Reports »
The National Health Insurance Act
Terms and Conditions of Use
Home
Contact Us
Search
Reset
Critical Care & Emergency Medicine | Novel Drugs & Emergent Therapeutics Archive 2023
View Novel Drugs & Emergent Therapeutics 2023 Archive
Currently reading
View Novel Drugs & Emergent Therapeutics 2024 Archive
Novel Drugs & Emergent Therapeutics Archive 2023
Date
Indication
Company
Drug / Device
Status
Title & Link
1
5/11/23
Paediatrics X-linked myotubular myopathy (XLMTM)
Astellis
AT132 (resamirigene bilparvovec)
AT132 IND and ASPIRO trial currently on clinical hold.
Astellis Pharma published preliminary results from APPIRO trial regarding safety and efficacy of investigational AT132 (resamirigene bilparvovec), an adeno-associated viral vector (AAV) gene replacement therapy designed to deliver a functional human MTM1 gene for the treatment of pediatric patients with X-linked myotubular myopathy (XLMTM).
ClinicalTrials.gov ID NCT03199469
09/11/23
Congenital thrombotic thrombocytopenic purpura (cTTP)
Takeda
Adzynma
Approved
FDA approves first recombinant protein product indicated for prophylactic (preventive) or on demand enzyme replacement therapy (ERT) in adult and pediatric patients with congenital thrombotic thrombocytopenic purpura
FDA Docket FDA-2014-D-1461
07/11/23
Sjogren's Syndrom
Amgen
Dazodalebep
Phase 2
Complete
Amgen presents new data from Phase 2 Trial of Dazodalebep in Sjogren's Syndrome
Phase 2 study
ClinicalTrials.gov. ID NCT04129164
20/09/23
Allergy, Anaphylaxis
ARS Pharma
Neffy
Approval Declined
US FDA declines to approve first nasal spray equivalent of EpiPen
14/07/23
Graft-vs-Host Disease
Syndax, Incyte
Axatilimab
Complete
Syndax and Incyte Announce Positive Topline Results from the Pivotal AGAVE-201 Trial of Axatilimab in Chronic Graft-Versus-Host Disease
Phase 2 Study,
ClinicalTrials.gov ID NCT04710576
19/09/23
Atopic Dermatitis
Arcutis
Roflumilast
Complete
Roflumilast Cream Effective in Pediatric Atopic Dermatitis Trial
Clinicaltrials.gov ID NCT04845620
28/07/23
Telemedicine, Respiratory Devices
U. Washington
Telemedicine, Monitoring
In trial
Smartphone system developed to measure oxygenation levels
24/07/23
HABP, VABP
Entasis Therapeutics
Xacdura
Approved
FDA grants approval for Xacdura for use in the treatment of ventilator-associated bacterial pneumonia
23/02/23
Haemophilia
Sanofi
Altuviiio
Approved
FDA approves Sanofi’s long-lasting hemophilia drug
18/11/22
Diabetes
Provention Bio
Tzield
Approved
Tzield: FDA approves first drug to delay type 1 diabetes
18/08/22
Beta-Thalassemia
BlueBird Bio
Zynteglo
Approved
Zynteglo Approved as First Gene Therapy for Beta-Thalassemia
18/03/22
Rare Diseases, CDKL5 Epilepsy
Marinus
ZTALMY® (ganaxolone)
Approved
Marinus Pharmaceuticals Announces FDA Approval of ZTALMY® (ganaxolone) for CDKL5 Deficiency Disorder
.
Rate
Viewed
Bookmark
Print
Rating
Rating Value
Most Viewed Articles
MNG004-World Health Organisation requests information from China regarding outbreak of respiratory diseases
Nov 23, 2023
CDC Flags BA.2.86 COVID Variant
Dec 04, 2023
Disease Outbreak News: Mpox (monkeypox)- Democratic Republic of the Congo
Nov 28, 2023
Rate This Media
×
1
2
3
4
5
Home
Contact Us
Log in
Powered by eLecture, a VisualLive Solution
© Copyright 2024
Terms of Use
Disclaimer
We use cookies to track how our site is used, but do not store any personal data. For more information, please review our Terms and Conditions.
I agree